Un muy importante estudio preclínico en ratones: cura para la anemia falciforme (rel. común en población con ancestral africana) usando #EdicionGenetica y #CRISPR. El futuro para el tx de enf. hemáticas hereditarias está próximo. https://t.co/W1I9hgd1la ht
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
RT @mighty_tora: CRISPR塩基編集により、鎌状赤血球症の原因となる遺伝子変異を病原性が無いMakassar型に書き換えて治療する@マウス。鎌状赤血球症の治療を目指す企業が複数あるが、このアプローチがbest-in-classになるかもしれない?🤔 鎌状赤血…
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
Spectacular. So many advances come together to make an incredible, elegant, (likely) permanent cure. Inspirational. Thank you, for the work, the share and the clear tweetorial!
RT @john_evans3: Beautiful @nature paper from labs of David Liu and Mitch Weiss showing base editing correction of the sickle mutation, lea…
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
I love a good science thread, and this is definitely one 👇🏻 Cool work with a great potential for patients
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
Very proud of this massive collaborative effort and humbled by the potential this genome editing strategy may have in helping sickle cell patients in the future! Read the deets from my PI below:
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @AkshaySharmaMD: Very proud of this collaboration with the @davidrliu lab. Look forward to moving this #BaseEditing strategy into a clin…
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
Base editing of haematopoietic stem cells rescues sickle cell disease in mice https://t.co/6kuddxsQYJ
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
Hopefully, this potential cure will make it the last few miles...
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @birloque: Más ejemplos de la nueva y espectacular medicina que tenemos a las puertas... Asombraos y predicad
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
We're in the early stages of an era of incredible advancements in health science.
RT @rjerala: Članek o popravilu mutacije v genu za hemoglobin, ki povzroča srpasto anemijo. Vsako leti se rodi 300.000 ljudi s to mutacijo,…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
This is huge as many white physicians fail to recognize the symptoms in their black patients
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @john_evans3: Beautiful @nature paper from labs of David Liu and Mitch Weiss showing base editing correction of the sickle mutation, lea…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
#SCGE PI @davidrliu published new research showing that base-editing of hematopoietic stem cells successfully rescued sickle cell disease in mice. Read the abstract in @Nature here: https://t.co/288ebVXmju 🧬
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @birloque: Más ejemplos de la nueva y espectacular medicina que tenemos a las puertas... Asombraos y predicad https://t.co/PNGD3qYmVv
Very proud of this collaboration with the @davidrliu lab. Look forward to moving this #BaseEditing strategy into a clinical trial for curing #SickleCell disease soon🤞🏽
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
Más ejemplos de la nueva y espectacular medicina que tenemos a las puertas... Asombraos y predicad
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
CRISPR塩基編集により、鎌状赤血球症の原因となる遺伝子変異を病原性が無いMakassar型に書き換えて治療する@マウス。鎌状赤血球症の治療を目指す企業が複数あるが、このアプローチがbest-in-classになるかもしれない?🤔 鎌状赤血球症の塩基編集治療薬であるBEAM-102は現在lead optimizationにある。
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
🤯🤯🤯🤯🤯🤯 …. Sont forts ces big pharma
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @davidrliu: Today we report in @Nature a base editing strategy that efficiently corrects the mutation in the β-globin gene HBB that caus…
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
CRISPR for the win
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
The finding of a rare human hemoglobin variant allows for the use of base editing to correct mutations causing sickle cell disease Very smart use of human genetics to overcome the limitations of $BEAM's technology
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
RT @EricTopol: The potential of a 1-shot #CRISPR base editing cure for sickle cell disease gets support and is exhilarating https://t.co/I0…
RT @john_evans3: Beautiful @nature paper from labs of David Liu and Mitch Weiss showing base editing correction of the sickle mutation, lea…