Plakophilin-2 (PKP2) gene therapy using AAV vector Grant US-11883506-B2 United States of America 30 Jan 2024
WPRE mutant constructs, compositions, and methods thereof Grant US-11851673-B2 United States of America 26 Dec 2023
Lentiviral vectors for delivery of PKLR to treat pyruvate kinase deficiency Grant US-11642422-B2 United States of America 09 May 2023
Methods of treating or preventing pyruvate kinase deficiency Grant US-11286501-B2 United States of America 29 Mar 2022
Composition for treatment of Crigler-Najjar syndrome Grant US-11241506-B2 United States of America 08 Feb 2022
WPRE MUTANT CONSTRUCTS, COMPOSITIONS AND METHODS THEREOF Application WO-2021183643-A1 World Intellectual Property Organisation (WIPO) 16 Sep 2021
GENE THERAPY FOR MAPLE SYRUP URINE DISEASE Application WO-2021170784-A1 World Intellectual Property Organisation (WIPO) 02 Sep 2021
RECOMBINANT VECTORS SUITABLE FOR THE TREATMENT OF IPEX SYNDROME Application WO-2020161122-A1 World Intellectual Property Organisation (WIPO) 13 Aug 2020
RECOMBINANT VECTORS SUITABLE FOR THE TREATMENT OF IPEX SYNDROME Application WO-2020104467-A1 World Intellectual Property Organisation (WIPO) 28 May 2020
Method for treating adenosine deaminase severe combined imunodeficiency Grant US-10583180-B2 United States of America 10 Mar 2020
CAR-expressing NK-92 cells as cell therapeutic agents Application US-10550197-B2 United States of America 04 Feb 2020
Modified hepatitis post-transcriptional regulatory elements Grant US-10363269-B2 United States of America 30 Jul 2019
Methods and compositions for increasing transgene activity Grant US-10179918-B2 United States of America 15 Jan 2019
Car-expressing NK-92 cells as cell therapeutic agents Application US-9920132-B2 United States of America 20 Mar 2018
MODIFIED HEPATITIS POST-TRANSCRIPTIONAL REGULATORY ELEMENTS Application WO-2016115177-A1 World Intellectual Property Organisation (WIPO) 21 Jul 2016