It's clear that #genetheraphy “is now giving rise to treatments for diseases that have not previously been treatable, & to life-altering treatments for diseases that had previously demanded Herculean efforts from the patient & the family.” #RareDis
Also see the companion article from Dr. Kathy High reviewing the last decade of gene therapy. https://t.co/egahS1YSfQ
In the past decade, gene and cell therapy products have provided new therapeutic options for single gene disorders and for hematologic malignancies. Informative @NatureComms review of promise and limitations. https://t.co/WbklzhG3Ct https://t.co/jfKImDFKm8
If we could ever identify the genetic cause of my wife’s immune condition, this would be swell.
🧬 A nice update on gene therapy '2.0' ...like the ring of "genes as medicines" :-) https://t.co/R9oSsjAVeP #openscience #datascience #bigdata #rstats #technology #biotech #itrtg #genomics #raredisease https://t.co/EMUZn1AXBO